Orphazyme trial update

Orphazyme recently announced that its interventional trial of Arimoclomal has achieved its recruitment target. The company has recruited 46 NPC patients in 8 countries for this 12 month placebo-controlled trial. There are two centres in the UK; Great Ormand Street and Birmingham.

William has been on the trial now for about 6 weeks (patients do not know if they are taking the Arimoclomal or the placebo). It is great news that patient recruitment has been completed because results will not be available until all the participants have completed the 12 month trial period.


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